V.H. CV#840A. Submitted to ASH 2001 Ann. Meet., 12/7-11, Orlando, FL. 
HEMATOLOGIC EPIGENETICS, GENOMICS, PROTEOMICS, & 1-CARBON METABOLISM 2002: SILENCING ìBADî AND ACTIVATING ìGOODî DNA, mRNA TRANSCRIPTS, AND THEIR PROTEINS, BY SELECTIVE TARGETED CHROMATIN METHYLATION AND DEMETHYLATION.
 Victor D. Herbert, MD, JD, MACP.  Mount Sinai-NYU Health System & Bronx V.A. Medical Center, Bronx, NY, 10468 United States.    
     Ever since Borek et al reported (1954) that when bacteria auxotrophic for methionine are deprived of methionine, their resultant less methylated RNA is under ìrelaxed controlî, i.e. is synthesized more rapidly, he, we, and many others have been gathering evidence that such ìrelaxed controlî also occurs in humans. Reviewing 3 decades of such evidence in our 1983 paper ìThe Inhibition of Some Cancers and the Promotion of Others by Folic Acid, Vitamin B12, and Their Antagonistsî (Herbert V. In: Nutritional Factors in the Induction and Maintenance of Malignancy [Butterworth CE Jr, Hutchinson ML, Eds.]. New York: Academic Press, 1983:273-287), including evidence that sickle cell disease could be ìtreatedî by producing folate deficiency, which activated a sharp rise in fetal hemoglobin and fall in sickle hemoglobin, we wrote, ìI should like to suggest the hypothesis that deficiency of folate or vitamin B12, or any other cause of failure to methylate DNA and/or RNA, can activate malignancy by hypomethylation of oncogenes, and that methylating oncogenes can inhibit malignancy by making them dormant.... Perhaps some of the second cancers that develop after successful antimetabolic chemotherapy are due to the same chemotherapy that directly destroys an active cancer, demethylating an oncogene of a dormant cancer.î With mapping of the genome, it has become clear that any DNA, RNA, or proteome allele, normal or variant, can be silenced by methylation or activated by demethylation  (due to methyl deficiency or demethylating agents such as 5-azacytidine).  As reviewed at the NIH August 6-8, 2001, Trans HHS Workshop, ìDiet, DNA Methylation Processes, and Healthî (In press, J Nutr, 2002 ) it is now clear that the repression of transcription by DNA methylation can occur through transcriptional repressive protein complexes (to which one can make inactivating antibodies) such as Dnmts (DNA methyltransferases) and HDACs (histone deacetylases). Hypermethylation is a double-edged sword: suppressing oncogenes and/or their product RNAs and/or proteins, and thereby suppressing cancer; and, conversely, suppressing the tumor suppressor genes, RNAs, and proteins which suppress angiogenesis and metastasis, and the DNA repair genes in malignant cells, thereby enhancing cancer growth and spread. Now that (A Wolffe, F Urnov, others [Trans HHS Workshop, vide supra]), one can selectively epigenetically silence by targeted methylation, with tailored zinc finger ìbulletsî, of its unique nucleotide sequences (single nucleotide polymorphisms) (SNPs, travelling in groups [haplotypes]) any gene variant chromatin target we wish, without methylating other genes, we are on the road, as we uncover their target nucleotide sequences (their promoter regions), to prevention and cure of all hematologic disorders associated with inherited or acquired gene variant chromatin that can be silenced by targeted methylation, including the myeloproliferative disorders, hemoglobinopathies, thalassemias, sideroblastic anemias, red cell enzyme defects, iron overload disorders, coagulation defects, and autoimmune disorders. Before clinical stigmata appear, one can isolate from the peripheral blood, by using microarray plates and other high-throughput genetic analysis instrumentation (C M Henry. Pharmacogenomics. Chem & Eng News, 2001; 79 (33): 37-42), not only these hematologic SNP targets but also non-hematologic targets, since even clinically undetectable early breast and prostate cancer constantly shed a few cells into the circulating blood (Trans HHS Workshop, vide supra).                  

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